Burosumab treatment in adults with X-linked hypophosphataemia: 96-week patient-reported outcomes and ambulatory function from a randomised phase 3 trial and open-label extension
Karine Briot, Anthony A Portale, Maria Luisa Brandi, Thomas O Carpenter, Hae Ii Cheong, Martine Cohen-Solal, Rachel K Crowley, Richard Eastell, Yasuo Imanishi, Steven Ing, Karl Insogna, Nobuaki Ito, Suzanne Jan de Beur, Muhammad K Javaid, Peter Kamenicky, Richard Keen, Takuo Kubota, Robin H Lachmann, Farzana Perwad, Pisit Pitukcheewanont, Stuart H Ralston, Yasuhiro Takeuchi, Hiroyuki Tanaka, Thomas J Weber, Han-Wook Yoo, Annabel Nixon, Mark Nixon, Wei Sun, Angela Williams, Erik A Imel
RMD Open Sep 2021, 7 (3) e001714; DOI: 10.1136/rmdopen-2021-001714
